Month: October 2016
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A review has been published about adrenoleukodystrophy (ALD), a rare, X-linked disorder of impaired very long-chain fatty acid metabolism. It focuses on the cerebral variant (cALD), which affects 35% of ALD patients in boyhood and causes rapid neurologic decline. It reviews the current perspectives of stem cell transplantation in cALD, which is the standard of care for early…